Rectifying function, restoring hope

Developing disease-modifying precision therapeutics for patients with serious genetic diseases


About us

Rectify is developing Positive Functional Modulators (PFMs), disease-modifying precision therapeutics that restore ABC transporter function for patients with serious genetic diseases.

ABC transporters are a 48-member family of membrane-bound proteins with etiologic loss-of-function mutations in multiple organ systems and therapeutic areas including the lungs, liver, gastrointestinal tract, eye, and central nervous system.

Our team


Scientific Advisory Board

Board of Directors


Join us

We are a team of passionate, driven scientists and biotech leaders, united in our vision to restore hope to individuals and families affected by serious genetic disease.

Rectify Pharma is looking for motivated individuals to join our growing team. Please click here to see our current openings or email for more information.

Contact us

400 Technology Square
Second floor, Suite 201
Cambridge, MA 02139